UCSF Pediatric Surgery
March 2, 2020
“This group of vulnerable patients has been relatively ignored in the fetal surgery world,” said UCSF’s Tippi MacKenzie, MD, senior author of the new study and member of the Eli and Edythe Broad Center for Regeneration Medicine and Stem Cell Research, who has worked for a decade developing novel therapies for heritable diseases that can be treated before birth. “We know these patients could potentially benefit from a number of medical therapies. So this is our first foray into treating one of those diseases.”